Exciting new gene and cell therapy technologies have the potential to treat devastating inherited diseases and rare disorders for which there is little hope of finding a conventional cure. Recent cutting-edge advances in genetic therapies are likely to provide game-changing treatments, if not cures, for many patients with rare inherited disorders.
Many speculate that advanced viral vector platforms are likely to reach the market in the next couple of years. In addition, optimism has been building in the industry following exciting recent breakthroughs in gene editing.
But how do we know if we’re there yet? Below are five industry trends that indicate that optimism is high in the gene therapy field and that we may very well see gene editing therapies for rare, and not so rare, disorders getting market approval in the very near future.